A question on #Vamorolone tabled by Freddie van Mierlo on 24-06-2025 has been answered by Karin Smyth.

Heading: Vamorolone
Question ID: 1816037
UIN: 62450
House: Commons
Date tabled: 2025-06-24
Asking Member ID: 5296
Asking Member display name: Freddie van Mierlo
Asking Member handle:
Asking Member Twitter reference: Freddie van Mierlo
Member interest: false
Question text: To ask the Secretary of State for Health and Social Care, how many patients have accessed Vamorolone since it was given NICE approval for Duchenne Muscular Dystrophy; what assessment he has made of the adequacy of availability of Vamorolone to patients wi
Is named day: true
Date of holding answer:
Date answered: 2025-06-30
Date answer corrected:
Is holding answer: false
Is correcting answer: false
Answering Member ID: 4444
Answering Member display name: Karin Smyth
Answering Member handle: karinsmyth
Answering Member Twitter reference: @karinsmyth
Correcting Member ID:
Correcting Member display name:
Correcting Member handle:
Correcting Member Twitter reference:
Answer text: The National Institute for Health and Care Excellence (NICE) published its technology appraisal, titled Vamorolone for treating Duchenne muscular dystrophy in people 4 years and over, on 16 January 2025. NHS England routinely commissioned vamorolone in li...
Original answer text:
Comparable answer text:
Answering body ID: 17
Answering body name: Department of Health and Social Care
Tweeted: true